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Mitochondrial Diseases - 27 Studies Found
Estado | Estudiar |
Terminated |
Nombre del estudio: RG2133 (2',3',5'-Tri-O-Acetyluridine) in Mitochondrial Disease Condición: Mitochondrial Diseases Fecha: 2003-05-07 Intervenciones: Drug: RG2133 (2',3',5'-tri-O-acetyluridine) |
Recruiting |
Nombre del estudio: An Observational Study of Patients With Primary Mitochondrial Disease (SPIMM-300) Condición: Primary Mitochondrial Disease Fecha: 2017-02-03 |
Active, not recruiting |
Nombre del estudio: A Study to Evaluate the Safety, Tolerability, and Efficacy of Subcutaneous Injections of Elamipretide (MTP-131) in Subjects With Genetically Confirmed Mitochondrial Disease Previously Treated in the Stealth BioTherapeutics SPIMM-201 Study Condición: Primary Mitochondrial Disease Fecha: 2016-06-13 Intervenciones:
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Completed |
Nombre del estudio: Energy Requirements in Mitochondrial Disease Condición:
Fecha: 2013-01-17 |
Completed |
Nombre del estudio: DINAMITE Study Nutritional State and Effect Diet in Mitochondrial Disease Condición: Mitochondrial Disorders Fecha: 2014-10-31 Intervenciones: Behavioral: diet intervention The dietary intervention implies optimizing the diet based on individually |
Completed |
Nombre del estudio: Open-Label, Dose-Escalating Study Assessing Safety, Tolerability, Efficacy, of RP103 in Mitochondrial Disease Condición: Inherited Mitochondrial Disease, Including Leigh Syndrome Fecha: 2013-12-17 Intervenciones: Drug: Cysteamine Bitartrate Cysteamine Bitartrate Delayed-release Capsules |
Recruiting |
Nombre del estudio: GDF-15 as a Biomarker for Mitochondrial Disease Condición:
Fecha: 2010-06-02 Intervenciones: Procedure: gastric emptying scan subjects will eat a solid |
Recruiting |
Nombre del estudio: North American Mitochondrial Disease Consortium Patient Registry and Biorepository (NAMDC) Condición:
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Active, not recruiting |
Nombre del estudio: EPI-743 for Mitochondrial Respiratory Chain Diseases Condición: Mitochondrial Diseases Fecha: 2011-06-07 Intervenciones: Drug: EPI-743 EPI-743 is administered as a dose escalation from 50 mg bid to 100 mg tid |